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IRDiRC - New rare disease research goals for the next decade

The International Rare Diseases Research Consortium (IRDiRC) - launched in 2011 has announce the new vision and goals for the next decade (2017-2027).

IRDiRC was originally conceived with two main goals: to contribute to the development of 200 new therapies and the means to diagnose most rare diseases by the year 2020. The last six years have seen considerable progress on these goals: the goal to deliver 200 new therapies was achieved in early 2017 - three years earlier than expected - and the goal for diagnostics is within reach.


In light of this, IRDiRC aims to initiate a year-long collaborative process to devise a new set of global rare disease goals for the upcoming decade, summarised as follows:


1. All patients coming to medical attention with a suspected rare disease will be diagnosed within one year if their disorder is known in the medical literature; all currently undiagnosable individuals will enter a globally coordinated diagnostic and research pipeline.

2. 1000 new therapies for rare diseases will be approved, the majority of which will focus on diseases without approved options.

3. Methodologies will be developed to assess the impact of diagnoses and therapies on rare disease patients



Link: http://www.irdirc.org



Last updated: Tuesday, August 22, 2017